A First-in-human Study to Learn About the Safety of BAY 3547926 and How Well it Works in Participants With Advanced Liver Cancer

Trial statusRecruiting
Trial phasePhase 1
Trial typeInterventional
Biological sexAll
Age18+
SponsorBayer

About this trial

In this study, researchers want to learn about the safety of a new drug, BAY 3547926, and how well the drug works in people with a type of liver cancer called advanced hepatocellular carcinoma (HCC), which has a special protein called Glypican 3 (GPC3). Researchers want to find the best dose of BAY 3547926 for people with advanced HCC and look at the way the body absorbs and distributes the drug.

The study drug, BAY 3547926, delivers a radioactive agent to cancer cells. The radioactive agent emits radiations which can damage the cancer cells and cause them to die. These radiations travel a small distance, so are expected to cause little damage to surrounding healthy tissues. This is the first study of BAY 3547926 in humans.

Participants will take part in one of the 4 different parts of the study. In Part 1, participants will receive different doses of BAY 3547926 alone to find the dose that is deemed safe and works best for the participants. When this dose has been found, a larger number of participants will receive BAY 3547926 alone in Part 2 or with other treatments in Parts 3 and 4 of the study.

During the study, the doctors and their study team will do health check-ups, take pictures (scans) of the body, collect blood and urine samples, and ask participants questions about how they are feeling and what health problems they are having.

Eligibility criteria

This trial does not accept healthy volunteers

Qualifiers

Locally advanced or metastatic and/or unresectable HCC (hepatocellular carcinoma) with histological or cytological confirmation, or non-invasive diagnosis as per American Association for the Study of Liver Diseases (AASLD) criteria in participants with a confirmed diagnosis of cirrhosis.

Demonstrated positive centrally confirmed GPC3 expression by immunohistochemistry (IHC) on tumor sample.

Disease not amenable to, or progressive disease after, curative surgery and/or locoregional therapies of established efficacy such as resection, local ablation, chemoembolization.

Eastern Cooperative Oncology Group (ECOG) Performance Status (PS) of 0 or 1.

Disqualifiers

Fibrolamellar HCC, sarcomatoid HCC, and mixed hepatocellular/cholangiocarcinoma subtypes.

Participants with a history or clinical evidence of CNS metastases, unless they meet specific criteria

History of encephalopathy ≥ Grade 2 within the past 12 months

Clinically significant ascites

Trial design

Design model

Single group

Treatments tested in this trial

  • BAY 3547926

    Drug

    antibody conjugate with actinium-225 label

  • BAY 3547922

    Drug

    antibody conjugate without actinium-225 label as preinjection

  • BAY 3713391

    Drug

    Radioactive imaging agent - optional preinjection

Treatment groups

148 Participants
are divided into 1 treatment group
Group A: BAY 3547926Experimental treatment 3 interventions

Trial outcomes

Primary outcomes

1

Part 1 (dose escalation): Occurrence and severity of TEAEs

TEAE=Treatment emergent adverse event

Time frame
up to 60 months after first administration
2

Part 1 (dose escalation): Recommended safe and active dose (RSAD)

The RSAD is based on incidence of DLT and preliminary anti-tumor activity (ORR using RECIST 1.1 by Investigator assessment) informed by TITE-CRM. RSAD=Recommended safe and active dose DLT=Dose limiting toxicity ORR=Objective reponse rate RECIST=Response Evaluation Criteria in Solid Tumors TITE-CRM =Time-to-event continual reassessment method

Time frame
up to 60 months after first administration
3

Part 2 (dose expansion): Occurrence and severity of TEAEs

TEAE=Treatment emergent adverse event

Time frame
up to 60 months after first administration
4

Part 2 (dose expansion): ORR using RECIST 1.1 by investigator assessment

ORR=Objective reponse rate RECIST=Response Evaluation Criteria in Solid Tumors

Time frame
up to 60 months after first administration

Secondary outcomes

1

Part 1 (dose escalation): Recommended dose level(s) based on occurrence and severity of TEAEs and DLTs, PK, immunogenicity, and preliminary anit-tumor activity (ORR using RECIST 1.1 by Investigator assessment)

TEAE=Treatment emergent adverse event DLT=Dose limiting toxicity PK=Pharmacokinetic ORR=Objective response rate RECIST=Response Evaluation Criteria in Solid Tumors

Time frame
up to 60 months after first administration
2

Part 1 (dose escalation): Recommended dosing regimen based on occurrence and severity of TEAEs and DLTs, PK, immunogenicity, and preliminary anti-tumor activity (ORR using RECIST 1.1 by Investigator assessment)

TEAE=Treatment emergent adverse event DLT=Dose limiting toxicity PK=Pharmacokinetic ORR=Objective response rate RECIST=Response Evaluation Criteria in Solid Tumors

Time frame
up to 60 months after first administration
3

Part 1 (dose escalation): ORR using RECIST 1.1 by investigator assessment

ORR=Objective response rate RECIST=Response Evaluation Criteria in Solid Tumors

Time frame
up to 60 months after first administration
4

Part 1 (dose escalation): DCR using RECIST 1.1 by investigator assessment

DCR=Disease control rate RECIST=Response Evaluation Criteria in Solid Tumors

Time frame
up to 60 months after first administration

Other outcomes

Sponsors and contacts

Click on the lead sponsor to view all of their trials.